RareBoost Seminar: Dr. Andrés F. Muro “Applications of CRISPR/Cas9 Technology for the Treatment of Rare Diseases”
We are pleased to invite you to the upcoming RareBoost Seminar by Dr. Andrés Fernando Muro, titled “Applications of CRISPR/Cas9 Technology for the Treatment of Rare Diseases”.
📅 Friday, September 19, 2025
🕚 11:00 AM
📍 IBG Aziz Sancar Auditorium (Hybrid format – in-person & online)
To join the seminar online, please register using the link: https://lu.ma/0i5eevii
We look forward to your participation!
About the Speaker
Dr. Muro earned his PHD degree in Biology from the School of Sciences, University of Buenos Aires, Buenos Aires, Argentina. He is the group leader of the Mouse Molecular Genetics Laboratory at the International Centre of Genetic Engineering and Biotechnology (ICGEB), Trieste, Italy.
Dr. Muro’s focus of research is the understanding of gene function and their relation to diseases, and the development of efficient therapeutic approaches, using mouse models, with special emphasis in metabolic liver diseases and possible therapies for neonatal hyperbilirubinemia and the Crigler-Najjar syndrome type.
He is interested in the understanding of the mechanisms of bilirubin neurotoxicity, to develop pharmacological and gene therapy approaches aimed to avoid severe and permanent brain damage, and lethality.
In parallel to the work in CNSI, he is developing a therapeutic vector to treat patients suffering from ornithine transcarbamylase deficiency. Dr. Muro is participating in international research and clinical networks aiming to transfer the developed therapies to the clinics.